Our drug development services, in even the rarest indications, support our clients and patients every step of the way.
That’s because everything we do, we do to improve patient quality of life.
That includes offering our clients a personal, tailored approach, building solid relationships and staying nimble in order to meet the changing needs of trials in small populations.
We build and execute successful trials by custom-building our services around sponsors and patients, while our expert team ensures patients are supported, by acknowledging the challenges in the clinical trial environment.
We look forward to talking with you, learning more about your specific goals and determining how we can help you.
The Rare Disease and Pediatric Center takes a different approach to study programs.
The Center enables us to deliver better recruitment, retention and compliance, and to provide the contextual research that regulators value.
By focusing on the individual, not just the rare disease, our team flexibly addresses needs on an individual basis, understanding disease progression and lived experience, while also demonstrating efficacy. We also leverage the commonalities across rare and pediatric research to make recruiting and retaining each person more efficient.
Skilled in engaging the caregivers in both areas, building relationships that benefit patient and family, we stay close to patients, addressing any issues quickly and effectively. And our senior leadership team
prioritize the needs of our patient communities, allowing us to step up and share the experiences that enrich our trial delivery approach.
We go beyond just running with a protocol, instead carrying out the forensic analysis that ensures a strategic approach from the beginning.
Our Center is…
- Built around individual patient needs and understanding the benefits for each one, from stabilization of a disease to a better quality of life, ensuring patient retention and thus better outcomes for sponsors.
- Able to mitigate the risks that can occur by being proactive in risk identification. Our individualized approach allows us to recognize improvements in individual patients and tailor the trial to obtain quantitative data/outcomes for our clients.
- Building a bridge over the drug development ‘valley of death’ often experienced by sponsors with other CRO partners, through our personal and industry experience within our leadership team.
Due to our non-linear approach to capturing efficacy, we can rescue vital research. This approach is both flexible and rigorous, allowing people to show stabilization/improvement in different ways.
Advancing pediatric care
We understand the additional considerations in the pediatric setting, working closely with sponsors to extend their evaluation from treatments already approved in adult populations.
And our understanding of the challenges in various age ranges enables us to problem solve with sponsors at each step of the trial journey, delivering what they need and meeting trial milestones.
Recruitment is one of the biggest challenges in pediatric research. We utilise our relationships alongside technology to build recruitment plans. In addition, we work closely with the client and the sites to design trials that enhance recruitment prospects.
Our patient-centered study designs are designed to meet the objectives outlined by the sponsor and the regulatory agencies.
Achieving more with less
When there are limited patient populations, our innovative study designs and statistical capabilities are critical.
The quality of our work and collaborative approach both add value, by shaping robust strategies and giving the expert insight that supports the drug development process. Our critical analysis is key to reviewing study protocols and informing trial decision-making.
Our approach is also designed to reduce burdens, obstacles and pain points, enabling increased efficiencies, enhancing cost-effectiveness, minimizing potential for extended FDA reviews and maximizing patient access to treatment.
Emmes Rare Disease and Pediatric Center
Respect for the patient is at the heart of everything we do. We look after people in the most appropriate and flexible way. That results in successful trials and outcomes for both patients and sponsors alike.